Status | Study |
Active, not recruiting |
Study Name: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Condition: Mucopolysaccharidosis Hurler Syndrome Date: 2010-01-05 Interventions: Drug: Campath-1H Administered |
Completed |
Study Name: Clinical Study of Aldurazyme in Patients With Mucopolysaccharidosis (MPS) I Condition: Mucopolysaccharidosis I Hurlers Syndrome Date: 2009-06-02 Interventions: Biological: rhIDU (recombinant human-Alpha-L-Iduronidase) |
Completed |
Study Name: Immune Tolerance Study With Aldurazyme® (Laronidase) Condition: Mucopolysaccharidosis I Date: 2008-08-13 Interventions: Biological: Laronidase 0.058 m |
Terminated |
Study Name: Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism Condition: Hurler's Syndrome Maroteaux-Lamy Syndrome Date: 2008-04-25 Interventions: Procedure: Stem Cell Transplantation |
Active, not recruiting |
Study Name: Intrathecal Enzyme Replacement for Hurler Syndrome Condition: Hurler Syndrome Date: 2008-03-11 Interventions: Drug: IRT Laronidase Laronidase belongs to a class of drug |
Recruiting |
Study Name: A Study of the Effect of Aldurazyme® (Laronidase) Treatment on Lactation in Female Patients With Mucopolysaccharidosis I (MPS I) and Their Breastfed Infants Condition: Mucopolysaccharidosis I Hurler's Syndrome Date: 2007-01-03 Interventions: Biological: Aldurazyme (laronidase) dose of 0.58mg/kg body weight intravenously (IV) every week |
Enrolling by invitation |
Study Name: Effects of Growth Hormone in Chronically Ill Children Condition: - Hurler Syndrome (MPS-1) With Short Stature and Muscle Wasting Date: 2006-02-01 Interventions: Drug: Growth Hormone Procedure: Whole body |
Completed |
Study Name: Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease Condition: Mucopolysaccharidosis I Hurler Syndrome Date: 2005-11-22 Interventions: Biological: Aldurazyme (Recombinant Human Alpha-L-Iduronidase) 0.58 mg/kg every week |
Completed |
Study Name: Stem Cell Transplant w/Laronidase for Hurler Condition: Mucopolysaccharidosis I Hurler Syndrome Date: 2005-09-12 Interventions: Procedure: Stem Cell Transplant |
Completed |
Study Name: Stem Cell Transplantation for Hurler Condition: Mucopolysaccharidosis I Mucopolysaccharidosis VI Mannosido Date: 2005-09-12 Interventions: Procedure: Stem Cell Transplant |